- OUTLOOK
- Correction 27 August 2020
After three decades of false starts, gene therapy against the disease is in new clinical trials — and there is even hope of a cure.
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- Roxanne Khamsi0
- Roxanne Khamsi
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When Katie Brady’s son was born, everything seemed normal. The hospital staff pricked his heel to get blood for a routine newborn screening test, and she and her husband waited for the result without much concern. The couple had three children already — all girls — and the only thing that seemed to set Henry apart from his siblings at birth was the fact that he was a boy.
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Nature 583, S12-S14 (2020)
doi: https://doi.org/10.1038/d41586-020-02111-z
This article is part of Nature Outlook: Cystic fibrosis, an editorially independent supplement produced with the financial support of third parties. About this content.
Updates & Corrections
-
Correction 27 August 2020: An earlier version of this Outlook article used the wrong pronoun when referring to Sriram Vaidyanathan.
References
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Drumm, M. L. et al. Cell 62, 1227–1233 (1990).
Rich, D. P. et al. Nature 347, 358–363 (1990).
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Maule, G. et al. Nature Commun. 10, 3556 (2019).
Geurts, M. H. et al. Cell Stem Cell 26, 503–510 (2020).
Vaidyanathan, S. et al. Cell Stem Cell 26, 161–171 (2020).
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